|
1
|
Acute Leukemia |
|
2
|
Adrenal Cancer -
with distant metastases or inoperable, unresectable or recurrent |
|
3
|
Alexander Disease (ALX) -
Neonatal and Infantile |
|
4
|
Amyotrophic Lateral Sclerosis (ALS) |
|
5
|
Anaplastic Adrenal Cancer -
with distant metastases or inoperable, unresectable or recurrent |
|
6
|
Astrocytoma -
Grade III and IV |
|
7
|
Bladder Cancer -
with distant metastases or inoperable or unresectable |
|
8
|
Bone Cancer -
with distant metastases or
inoperable or unresectable |
|
9
|
Breast Cancer -
with distant metastases or
inoperable or unresectable |
|
10
|
Canavan Disease (CD) |
|
11
|
Cerebro Oculo Facio Skeletal (COFS)
Syndrome |
|
12
|
Chronic Myelogenous Leukemia (CML) -
Blast Phase |
|
13
|
Creutzfeldt-Jakob Disease (CJD) -
Adult |
|
14
|
Ependymoblastoma
(Child Brain Tumor) |
|
15
|
Esophageal Cancer |
|
16
|
Farber's Disease (FD) -
Infantile |
|
17
|
Friedreichs Ataxia (FRDA) |
|
18
|
Frontotemporal Dementia (FTD), Picks
Disease -Type A - Adult |
|
19
|
Gallbladder Cancer |
|
20
|
Gaucher Disease (GD) -
Type 2 |
|
21
|
Glioblastoma Multiforme
(Brain Tumor) |
|
22
|
Head and Neck Cancers -
with distant metastasis or
inoperable or uresectable |
|
23
|
Infantile Neuroaxonal Dystrophy (INAD) |
|
24
|
Inflammatory Breast Cancer (IBC) |
|
25
|
Kidney Cancer -
inoperable or unresectable |
|
26
|
Krabbe Disease (KD) -
Infantile |
|
27
|
Large Intestine Cancer -
with distant metastasis or
inoperable, unresectable or recurrent |
|
28
|
Lesch-Nyhan Syndrome (LNS) |
|
29
|
Liver Cancer |
|
30
|
Mantle Cell Lymphoma (MCL) |
|
31
|
Metachromatic Leukodystrophy (MLD) -
Late Infantile |
|
32
|
Niemann-Pick Disease (NPD) -
Type A |
|
33
|
Non-Small Cell Lung Cancer -
with metastases to or beyond the
hilar nodes or inoperable, unresectable or recurrent |
|
34
|
Ornithine Transcarbamylase (OTC)
Deficiency |
|
35
|
Osteogenesis Imperfecta (OI) -
Type II |
|
36
|
Ovarian Cancer -
with distant metastases or
inoperable or unresectable |
|
37
|
Pancreatic Cancer |
|
38
|
Peritoneal Mesothelioma |
|
39
|
Pleural Mesothelioma |
|
40
|
Pompe Disease -
Infantile |
|
41
|
Rett (RTT) Syndrome |
|
42
|
Salivary Tumors |
|
43
|
Sandhoff Disease |
|
44
|
Small Cell Cancer (of the Large
Intestine, Ovary, Prostate, or Uterus) |
|
45
|
Small Cell Lung Cancer |
|
46
|
Small Intestine Cancer -
with distant metastases or
inoperable, unresectable or recurrent |
|
47
|
Spinal Muscular Atrophy (SMA) -
Types 0 And 1 |
|
48
|
Stomach Cancer -
with distant metastases or
inoperable, unresectable or recurrent |
|
49
|
Thyroid Cancer |
|
50
|
Ureter Cancer - with distant
metastases or inoperable, unresectable or recurrent |
